Indication
Late-Infantile Neuronal Ceroid Lipofuscinosis
1 clinical trial
1 product
Product
AT-GTX-501Clinical trial
Phase I/IIa Gene Transfer Clinical Trial for Variant Late Infantile Neuronal Ceroid Lipofuscinosis, Delivering the CLN6 Gene by Self-Complementary AAV9Status: Completed, Estimated PCD: 2021-10-27