Product
AT-GTX-501
2 clinical trials
3 indications
Indication
Ceroid Lipofuscinosis 6Indication
Batten DiseaseClinical trial
Phase I/IIa Gene Transfer Clinical Trial for Variant Late Infantile Neuronal Ceroid Lipofuscinosis, Delivering the CLN6 Gene by Self-Complementary AAV9Status: Completed, Estimated PCD: 2021-10-27
Clinical trial
Long-Term Follow-Up of AT-GTX-501 scAAV9 Gene Transfer in Subjects With CLN6 Batten DiseaseStatus: Active (not recruiting), Estimated PCD: 2024-10-01