Indication
Hyperphenylalaninemia
1 clinical trial
1 product
Clinical trial
A Phase 1/2, Open-Label, Randomized Parallel Arm, Intra-patient Dose Escalation Study to Evaluate the Safety, Pharmacokinetics and Preliminary Efficacy of CNSA-001(Sepiapterin) in Primary Tetrahydrobiopterin Deficient Patients With HyperphenylalaninemiaStatus: Completed, Estimated PCD: 2020-10-02
Product
PTC923