Product
PTC923
Aliases
Sepiapterin
3 clinical trials
3 indications
Indication
PhenylketonuriaIndication
BH4 DeficiencyIndication
HyperphenylalaninemiaClinical trial
A Phase 3 Study of PTC923 in Subjects With PhenylketonuriaStatus: Completed, Estimated PCD: 2023-04-03
Clinical trial
A Phase 3 Open-Label Study of PTC923 (Sepiapterin) in PhenylketonuriaStatus: Recruiting, Estimated PCD: 2025-02-07
Clinical trial
A Phase 1/2, Open-Label, Randomized Parallel Arm, Intra-patient Dose Escalation Study to Evaluate the Safety, Pharmacokinetics and Preliminary Efficacy of CNSA-001(Sepiapterin) in Primary Tetrahydrobiopterin Deficient Patients With HyperphenylalaninemiaStatus: Completed, Estimated PCD: 2020-10-02