Indication

Late-Onset Pompe Disease (LOPD)

1 clinical trial

1 product

Clinical trial

Phase 1/2, Dose-escalation Study to Evaluate the Safety, Tolerability and Efficacy of a Single Intravenous Infusion of SPK-3006 in Adults With Late-onset Pompe Disease

Status: Active (not recruiting), Estimated PCD: 2032-04-01

Product