Product
SPK-3006
1 clinical trial
5 indications
Indication
Pompe DiseaseIndication
Glycogen Storage Disease Type 2Indication
Late-Onset Pompe Disease (LOPD)Indication
Lysosomal Storage DiseasesIndication
Glycogen Storage Disease Type IIClinical trial
Phase 1/2, Dose-escalation Study to Evaluate the Safety, Tolerability and Efficacy of a Single Intravenous Infusion of SPK-3006 in Adults With Late-onset Pompe DiseaseStatus: Active (not recruiting), Estimated PCD: 2032-04-01