Product
Adjuvant Immunosuppression Therapy
Aliases
Adjuvant Immunosuppression (IS) Therapy
2 clinical trials
5 indications
Indication
Mucopolysaccharidosis type IIIAIndication
Sanfilippo syndromeIndication
Mucopolysaccharidosis type IIIIndication
MPS IIIIndication
MPS III-AClinical trial
Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH for Mucopolysaccharidosis (MPS) IIIAStatus: Active (not recruiting), Estimated PCD: 2024-06-01
Clinical trial
A Long-term Follow-up Study of Patients With MPS IIIA From Gene Therapy Clinical Trials Involving the Administration of ABO-102 (scAAV9.U1a.hSGSH)Status: , Estimated PCD: 2027-06-01