Indication
MPS III-A
2 clinical trials
4 products
Clinical trial
A Long-term Follow-up Study of Patients With MPS IIIA From Gene Therapy Clinical Trials Involving the Administration of ABO-102 (scAAV9.U1a.hSGSH)Status: , Estimated PCD: 2027-06-01
Product
Adjuvant ImmunosuppressionClinical trial
Phase I/II Study of Weekly Infusions of JR-441 in Patients With Mucopolysaccharidosis Type IIIAStatus: Recruiting, Estimated PCD: 2029-10-31
Product
JR-441