Product
SRP-9003
Aliases
scAAVrh74.MHCK7.hSGCB, scAAVrh74.MHCK7.hSGCB, bidridistrogene xeboparvovec
3 clinical trials
4 indications
Indication
Limb-girdle Muscular DystrophyIndication
Limb-girdle muscular dystrophyIndication
Type 2EIndication
Limb-Girdle Muscular DystrophyClinical trial
A Phase 3 Multinational, Open-label, Systemic Gene Delivery Study to Evaluate the Safety and Efficacy of SRP-9003 in Subjects With Limb Girdle Muscular Dystrophy 2E/R4Status: Recruiting, Estimated PCD: 2025-01-31
Clinical trial
A Single-Center, Open-Label, Systemic Gene Delivery Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9003 Administered by Systemic Infusion in Subjects With LGMD2E (β-Sarcoglycan Deficiency)Status: Active (not recruiting), Estimated PCD: 2027-02-14
Clinical trial
A Multicenter, Open-label, Single-dose, Systemic Gene Transfer Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9003 on Subjects With Limb Girdle Muscular Dystrophy, Type 2E/R4 (β-Sarcoglycan Deficiency)Status: Active (not recruiting), Estimated PCD: 2028-08-28