Indication
Limb-girdle muscular dystrophy
3 clinical trials
3 products
Product
SRP-9003Clinical trial
A Single-Center, Open-Label, Systemic Gene Delivery Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9003 Administered by Systemic Infusion in Subjects With LGMD2E (β-Sarcoglycan Deficiency)Status: Active (not recruiting), Estimated PCD: 2027-02-14
Clinical trial
A Two-part Multicenter Study: a Randomized, Double-blind, Placebo-controlled Dose-escalation Safety Phase (Part 1) Followed by Double-blind, Placebo-controlled, Adaptive Phase (Part 2) Study to Evaluate the Safety and Efficacy of AB-1003 in Adult Subjects With LGMD2I/R9 Mutations in the Gene Encoding Fukutin Related Protein (FKRP)Status: Recruiting, Estimated PCD: 2028-12-01
Product
AB-1003Clinical trial
Phase I/IIA Gene Transfer Clinical Trial for LGMD2D (Alpha-Sarcoglycan Deficiency) Using scAAVrh74.tMCK.hSGCAStatus: Completed, Estimated PCD: 2019-03-14
Product
SRP-9004