Product
Adjuvant Immunosuppression (IS) Therapy
1 clinical trial
1 indication
Indication
MPS III-AClinical trial
A Long-term Follow-up Study of Patients With MPS IIIA From Gene Therapy Clinical Trials Involving the Administration of ABO-102 (scAAV9.U1a.hSGSH)Status: , Estimated PCD: 2027-06-01